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Press Releases
Apertura Gene Therapy Supports the Broad Institute in Development of Gene Therapy for Prion Disease Using Engineered AAV Capsid Targeting TfR1 for CNS Delivery
The prion program utilizes Apertura's preclinical development data with an AAV capsid targeting human Transferrin Receptor 1 (TfR1) to provide a roadmap for rapid advancement to the clinicUnique gene therapy
